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复旦科研团队研发亨廷顿舞蹈症潜在新药 - 2019年11月01日
Fudan research offers hope for Huntington's sufferers
Local researchers have found a way of activating cells to selectively "eat" the protein responsible for Huntington's disease, raising hopes for hundreds of thousands of patients around the world.
Researchers at Fudan University have found four compounds, described as "small molecule glue," which tether the mutant disease protein so it can’t escape cells that can eat themselves.
It is likely they can be developed into oral medication, said Lu Boxun, a professor at the university’s School of Life Sciences.